Sarepta Therapeutics, Inc. is a commercial-stage biopharmaceutical company focused on the discovery and development of RNA-targeted therapeutics, gene therapies, and other genetic therapeutic modalities for the treatment of rare diseases. The company offers EXONDYS 51 injection for the treatment of Duchenne muscular dystrophy in patients with confirmed mutation of the dystrophin gene amenable to exon 51 skipping, and VYONDYS 53 for the treatment of Duchenne in patients with confirmed mutation amenable to exon 53 skipping. Sarepta is also developing AMONDYS 45, a product candidate using phosphorodiamidate morpholino oligomer chemistry and exon-skipping technology to skip exon 45 of the dystrophin gene; SRP-5051, a peptide conjugated PMO that binds exon 51 of dystrophin pre-mRNA; SRP-9001, a DMD micro-dystrophin gene therapy program; and SRP-9003, a limb-girdle muscular dystrophies gene therapy program. The company has collaboration agreements with F. Hoffman-La Roche Ltd, Nationwide Children's Hospital, Lysogene, Duke University, Genethon, and StrideBio. Sarepta was incorporated in 1980 and is headquartered in Cambridge, Massachusetts.
| Symbol | SRPT |
|---|---|
| Exchange | NASDAQ |
| Sector | Healthcare |
| Industry | Biotechnology |
| CEO | Douglas S. Ingram |
| Employees | 1372 |
| Headquarters | Cambridge, MA, US |
| IPO | 1997-06-04 |
| Website | www.sarepta.com |